News
Sarepta Therapeutics is pausing shipments of its gene therapy for muscular dystrophy following several patient deaths that ...
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MedPage Today on MSNGene Therapy May Hold Better Outcomes for Congenital Deafness Than Cochlear Implant
Youth with congenital deafness treated with gene therapy showed better progress on certain hearing measures than counterparts ...
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News-Medical.Net on MSNBreakthrough gene therapy reverses genetic deafness across age groups
Using gene therapy to treat hereditary deafness is safe and effective in both children and adults, according to new findings ...
BioMarin's Roctavian gene therapy shows long-term effectiveness in treating severe hemophilia A, reducing bleeding and ...
RDH12, a gene therapy for RDH12-associated Leber congenital amaurosis (RDH12-LCA) RESEARCH TRIANGLE PARK, N.C., July 23, 2025 ...
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News Medical on MSNUC Davis researchers pioneer safer gene therapy for vision loss
The UC Davis Department of Ophthalmology has received a five-year, $3.6 million grant from the National Eye Institute to ...
The Vision Center at Children’s Hospital Los Angeles is developing a protocol for a phase 1 clinical trial for the first gene ...
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MedPage Today on MSNCancer Drugs for Alzheimer's? Gene Therapy Distribution Halted; Reframing APOE4
Sarepta Therapeutics said it will temporarily pause all shipments of delandistrogene moxeparvovec (Elevidys) for Duchenne ...
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