Adeno-associated viruses (AAVs) have emerged as essential tools for delivering genetic material into tissues and engineering therapeutic cells. As gene and cell therapies advance, researchers optimize ...

A UCSF and Gladstone Institutes team discovered a pair of cancer drugs that successfully treated a model of severe ...

Prime editing corrects the most common genetic mutations that cause alternating hemiplegia of childhood (AHC), a rare and severe neurological disorder.

A study comparing the gene expression signature of Alzheimer's disease with those elicited by 1,300 approved drugs found a combination of two cancer ...

The Centers for Medicare & Medicaid Services (CMS) has unveiled a groundbreaking initiative aimed at expanding access to ...

Amid a season of regulatory and scientific advances, experts reveal a culture of data hoarding among cell and gene therapy ...